October 06, 2025 Spruce Biosciences Receives U.S. FDA Breakthrough Therapy Designation for Tralesinidase Alfa Enzyme Replacement Therapy (TA-ERT) in Sanfilippo Syndrome Type B (MPS IIIB)
September 30, 2025 Vicore Pharma – Buloxibutid Receives Orphan Drug Designation in Japan for the Treatment of Idiopathic Pulmonary Fibrosis
September 30, 2025 Gesynta Pharma receives UK approval for a Phase 2 trial of vipoglanstat in endometriosis
September 25, 2025 Aro Biotherapeutics Completes Enrollment in Phase 1b Trial of Targeted siRNA Therapy, ABX1100, in Late-Onset Pompe Disease (LOPD)
September 03, 2025 Pretzel Therapeutics Strengthens Leadership with Appointment of Ashish Dugar, Ph.D., MBA as Chief Development Officer
September 02, 2025 Hemab Therapeutics Expands Leadership with Appointment of Anant Murthy, PhD, as Chief Operating Officer
September 01, 2025 Oncopeptides – New real-world data confirms efficacy and safety of Pepaxti, presented at IMS Annual Meeting