April 17, 2019 GenSight Biologics reports positive follow-up results at Week 72 of the RESCUE Phase III clinical trial of GS010 in Leber Hereditary Optic Neuropathy (LHON)
April 16, 2019 Aprea Therapeutics Receives FDA Fast Track Designation and Orphan Drug Designation for APR-246 for the Treatment of Myelodysplastic Syndromes (MDS)
April 15, 2019 Strongbridge Biopharma plc Announces Upcoming Presentation of New Data from Phase 3 SONICS Study of RECORLEV™ (levoketoconazole) for the Treatment of Endogenous Cushing’s Syndrome at the 2019 American Association of Clinical Endocrinologists (AACE) Annual
April 11, 2019 Altimmune To Present NasoVAX Phase 2 Data at the World Vaccine Congress in Washington, D.C.